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To date, there is still no definitive cure for cblC. Nonostante il trattamento farmacologico riesca a mantenere nel breve periodo un buon controllo metabolico, la prognosi a medio e lungo termine rimane sfavorevole, con progressivo deterioramento neurologico e retinico.

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You can also support research with a bank or postal donation made out to:

Methylmalonic Acidemia with Homocystinuria Italian Association cblC aps

Bank Details

IBAN: IT30I0623003201000064380273
Crédit Agricole Italia
Agenzia N.2 di Roma – Viale Regina Margherita, 188

code BIC/SWIFT CRPPIT2P595

Postal Details

Postal Account: 1040047332
IBAN: IT61Z0760103200001040047332